A new study has answered a question that has puzzled cancer researchers for decades: Does a genetic defect found in nearly ...

Why are some people unable to hear from birth, even though their inner ear appears intact? One possible cause lies in the ...

Gene Shalit rang in his 100th birthday with a special tribute from the ‘Today' family and shared a recent photo amid his ...

A growing body of evidence suggests that a single gene, APOE, may play a far more dominant role in Alzheimer’s disease than ...

Though the therapy, Kresladi, isn’t seen as a big seller, its clearance is a step forward for a company that’s lost most of ...

With an end-of-week green light from the FDA, Rocket Pharmaceuticals has officially broken into commercial orbit.  | Rocket ...

While RNA sequencing (RNA-seq) has become a standard tool for profiling which genes are active in an organism, determining ...

Full 12-month data from Ocugen’s phase 2 eye disease gene therapy show the therapy significantly reduces the size of lesions, ...

Researchers at the Yong Loo Lin School of Medicine, National University of Singapore (NUS Medicine) have developed a ...

A first-in-human clinical trial evaluating an investigational gene therapy targeting complement-mediated pathways in ...

Upon approval, Rocket has been awarded a priority review voucher, which currently fetch around $200m on the secondary market.